Therapeutic Oligonucleotides Targeting Liver Disease: TTR Amyloidosis

Niemietz, Christoph, Chandhok, Gursimran, Schmidt, Hartmut
2015

Dual strategies to correct abnormal ion transports in cystic fibrosis using construct therapy

Kolonko, Anna Katharina
2019

Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells

Niemietz, Christoph, Sauer, Vanessa Daniela, Stella, Jaqueline, Fleischhauer, Lutz, Chandhok, Gursimran, Guttmann, Sarah, Avsar, Yesim, Guo, Shuling, Ackermann, Elisabeth J., Gollob, Jared, Monia, Brett P., Zibert, Andree, Schmidt, Hartmut
2016